CAMP4 Therapeutics Corporation, a biotechnology firm, was established in 2015 by Richard A. Young and Leonard Zon. Based in Cambridge, Massachusetts, its core focus is the identification and development of new therapeutic solutions for patients.
CAMP4 Therapeutics Receives Authorization in the United Kingdom for Phase 1/2 Human Clinical Trial of CMP-002 in Patients with SYNGAP1-Related Disorder
CAMP4 Therapeutics received UK MHRA authorization to add UK sites to its global Phase 1/2 clinical trial of CMP-002, its lead antisense oligonucleotide candidate for SYNGAP1-related disorder.
The clearance builds on July 2026 authorizations from Australia's TGA/HREC and Argentina's ANMAT, and the company remains on track to initiate the first-in-human study in Q4 2026; EU filings are still under review.
CMP-002 is positioned as a potential first-in-class disease-modifying therapy for a condition affecting over 10,000 people in the US with no approved disease-modifying treatments.